About NNZ-2591

NNZ-2591, an investigational drug (not approved by a regulatory body), is a synthetic version of a substance that occurs naturally in our brains, which plays a role in regulating communication between nerve cells and reducing inflammation in the brain. The aim of treatment with NNZ-2591 is to improve communication between nerve cells, which could help with symptoms of Phelan-McDermid Syndrome.

NNZ-2591 is provided as a liquid to be taken by mouth, twice each day.